PPMD
 United States  / New Jersey  |  Research/Dev

To improve the treatment, quality of life, and long-term outlook for all individuals affected by Duchenne muscular dystrophy (Duchenne) through research, advocacy, education, and compassion.

Parent Project Muscular Dystrophy (PPMD) is the largest nonprofit organization in the United States focused entirely on Duchenne. We take a comprehensive approach in the fight against Duchenne—funding research, raising awareness, promoting advocacy, connecting the community, and broadening treatment options. PPMD continues to support the clinical trials of PTC124, a new small-molecule drug that could potentially treat Duchenne patients with premature stop codons. Because PPMD believes that every family that contacts us should have access to all of the information and help available, we do not have an automated phone system. Instead, every person who calls speaks with someone who can answer questions.

Research

Advocacy

Education

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